Which of the following is a potential benefit of gene editing (e.g., using CRISPR) over traditional gene addition therapy?
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Correct answer: It corrects the mutation directly at its native gene locus
Gene editing (e.g. CRISPR) can correct or disrupt a mutation directly at its native locus, restoring normal gene function and regulation, rather than adding a separate working copy as in traditional gene-addition therapy.
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More Gene therapy basics questions
- What is a major concern associated with genome-editing gene therapy methods like CRISPR in clinical application?
- Which of the following is NOT a major type of gene therapy approach?
- Why is tissue-specific targeting an important consideration when designing gene therapy vectors?
- Which of the following is a non-viral method of gene delivery in gene therapy?
- What is the difference between gene therapy and traditional drug therapy?
- Which of the following diseases would be most amenable to gene therapy using ex vivo modification of hematopoietic stem cells?