Which of the following best describes why a “perfect vector” for gene therapy does not yet exist?
Show answer and explanation
Correct answer: Because every vector trades off efficiency, capacity, targeting, and safety
Every delivery vector has trade-offs — viral vectors may integrate unpredictably or provoke immune responses, while non-viral methods may be inefficient or poorly targeted — so no single vector is universally optimal.
Keep practicing
More Gene therapy basics questions
- How can gene therapy address diseases caused by a dominant negative mutation (where a mutant gene product interferes with normal function)?
- Which statement about non-viral gene delivery systems is correct compared to viral vectors?
- Which gene therapy approach could potentially treat a recessive loss-of-function genetic disease by restoring missing protein function?
- Which of the following is an advantage of using in vivo gene therapy over ex vivo gene therapy?
- Why is immune response a major concern in gene therapy using viral vectors?
- What is the primary goal of gene therapy?