What is the primary goal of gene therapy?
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Correct answer: To modify a person’s genes to treat or cure a disease
Gene therapy aims to modify a person's genes — adding, replacing, or editing genetic material — to treat or cure disease. This distinguishes it from dietary, transplant, or antibody-based approaches.
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More Gene therapy basics questions
- Which of the following is the most common type of delivery vector used in gene therapy?
- Which of the following describes an “in vivo” gene therapy approach?
- Which strategy describes “ex vivo” gene therapy?
- Which viral vector type is particularly favored for gene therapy because it typically does not integrate into the host genome, reducing ris…
- What is one major limitation of AAV vectors in gene therapy?
- Which of the following is a potential benefit of gene editing (e.g., using CRISPR) over traditional gene addition therapy?