Inborn Errors of Metabolism · USMLE Step 1

Which of the following is the most accurate general definition of an inborn error of metabolism (IEM)?

  1. Inherited structural protein defects that cause immunodeficiency
  2. Inherited enzyme defects that impair metabolic pathways
  3. Chromosomal abnormalities producing major organ malformations
  4. Acquired metabolic disturbances due to dietary deficiency states
Show answer and explanation

Correct answer: Inherited enzyme defects that impair metabolic pathways

IEMs are genetic (often autosomal recessive) disorders caused by enzyme defects that disrupt biochemical pathways, resulting in accumulation of substrates or lack of necessary products.

Difficulty: Medium Question 7 of 19

Practice all 19 Inborn Errors of Metabolism questions

Keep practicing

More Inborn Errors of Metabolism questions