Inborn Errors of Metabolism · USMLE Step 1

A patient with an inborn error of metabolism affecting carbohydrate storage presents with severe fasting hypoglycemia and lactic acidosis. Which category does this most likely belong to?

  1. Amino acidopathy such as phenylketonuria
  2. A fatty acid oxidation disorder of beta-oxidation
  3. Glycogen storage disease (glycogen metabolism disorder)
  4. A urea cycle enzyme deficiency defect
Show answer and explanation

Correct answer: Glycogen storage disease (glycogen metabolism disorder)

Glycogen storage diseases affect the ability to mobilize stored glycogen during fasting; impaired glycogenolysis or gluconeogenesis can lead to hypoglycemia and lactic acidosis.

Difficulty: Medium Question 10 of 19

Practice all 19 Inborn Errors of Metabolism questions

Keep practicing

More Inborn Errors of Metabolism questions